Ildikó Enyedi, Hungarian director of Oscar-nominated “On Body and Soul” and 2020 Cannes contender “The Story of My Wife,” ...

Naruto Uzumaki, the celebrated ninja, began life as a lonely orphan, shunned by his village due to the Nine-Tailed Fox sealed ...

Toop-line data from RISE UP, a clinical trial testing Agios' mitapivat for treating sickle cell disease, is expected by ...

President Trump recently signed a wide-ranging executive order urging Congress to amend a crucial provision of a Biden-era ...

Orphan drug developers face significant difficulties when navigating market access frameworks in Europe. Could greater use of ...

Announced Positive Clinical Data for Adult and Pediatric Netherton Patients ASHBURN, Va., May 13, 2025 (GLOBE NEWSWIRE) -- ...

Company advancing plans to develop TPI 287, a novel, late stage abeotaxane that appears to cross the blood-brain barrier and has published clinical efficacy data in glioblastoma multiforme (GBM)Manage ...

The European Commission (EC) has granted orphan drug designation to Biodexa Pharmaceuticals’ oral tablet formulation of ...

The Panhandle Orphan Care Network works to support foster families ...